日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intra-amniotic antisense oligonucleotide treatment improves phenotypes in preclinical models of spinal muscular atrophy

羊膜腔内反义寡核苷酸治疗可改善脊髓性肌萎缩症临床前模型的表型

Borges, Beltran; Brown, Stephen M; Chen, Wan-Jin; Clarke, Maria T; Herzeg, Akos; Park, Jae Hong; Ross, Joshua; Kong, Lingling; Denton, Madeline; Smith, Amy K; Lum, Tony; Zada, Fareha Moulana; Cordero, Marco; Gupta, Nalin; Cook, Sarah E; Murray, Heather; Matson, John; Klein, Stephanie; Bennett, C Frank; Krainer, Adrian R; MacKenzie, Tippi C; Sumner, Charlotte J

In utero genetic therapy: Treatment of early onset neurological disorders before they start

子宫内基因治疗:在神经系统疾病早期发作前进行治疗

Borges, Beltran; Brown, Stephen M; MacKenzie, Tippi C; Sumner, Charlotte J

Hypothermia Shifts Neurodegeneration Phenotype in Neonatal Human Hypoxic-Ischemic Encephalopathy but Not in Related Piglet Models: Possible Relationship to Toxic Conformer and Intrinsically Disordered Prion-like Protein Accumulation.

低温可改变新生儿人类缺氧缺血性脑病的神经退行性表型,但对相关仔猪模型无影响:可能与毒性构象体和内在无序朊病毒样蛋白的积累有关

Martin Lee J, Lee Jennifer K, Niedzwiecki Mark V, Amrein Almira Adriana, Javdan Cameron, Chen May W, Olberding Valerie, Brown Stephen M, Park Dongseok, Yohannan Sophie, Putcha Hasitha, Zheng Becky, Garrido Annalise, Benderoth Jordan, Kisner Chloe, Ghaemmaghami Javid, Northington Frances J, Kratimenos Panagiotis

Onasemnogene-abeparvovec administration to premature infants with spinal muscular atrophy

对患有脊髓性肌萎缩症的早产儿使用Onasemnogene-abeparvovec

Brown, Stephen M; Ajjarapu, Aparna S; Ramachandra, Divya; Blasco-Pérez, Laura; Costa-Roger, Mar; Tizzano, Eduardo F; Sumner, Charlotte J; Mathews, Katherine D

A multi-domain fragment of Nogo-A protein is a potent inhibitor of cortical axon regeneration via Nogo receptor 1

Nogo-A 蛋白的多结构域片段是通过 Nogo 受体 1 抑制皮质轴突再生的有效抑制剂

Eric A Huebner, Byung G Kim, Philip J Duffy, Rebecca H Brown, Stephen M Strittmatter