日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Computational identification of small molecules for increased gene expression by synthetic circuits in mammalian cells.

利用合成回路在哺乳动物细胞中计算鉴定可增强基因表达的小分子

Pisani M, Calandra F, Rinaldi A, Cella F, Tedeschi F, Boffa I, Vozzi D, Brunetti-Pierri N, Carissimo A, Napolitano F, Siciliano V

DNA methylation epi-signature is associated with two molecularly and phenotypically distinct clinical subtypes of Phelan-McDermid syndrome

DNA甲基化表观遗传特征与Phelan-McDermid综合征的两种分子和表型不同的临床亚型相关。

Schenkel, L C; Aref-Eshghi, E; Rooney, K; Kerkhof, J; Levy, M A; McConkey, H; Rogers, R C; Phelan, K; Sarasua, S M; Jain, L; Pauly, R; Boccuto, L; DuPont, B; Cappuccio, G; Brunetti-Pierri, N; Schwartz, C E; Sadikovic, B

SR-A and SREC-I binding peptides increase HDAd-mediated liver transduction

SR-A 和 SREC-I 结合肽可增强 HDAd 介导的肝脏转导。

Piccolo, P; Annunziata, P; Mithbaokar, P; Brunetti-Pierri, N

Retinal transduction profiles by high-capacity viral vectors

高容量病毒载体对视网膜的转导特性

Puppo, A; Cesi, G; Marrocco, E; Piccolo, P; Jacca, S; Shayakhmetov, D M; Parks, R J; Davidson, B L; Colloca, S; Brunetti-Pierri, N; Ng, P; Donofrio, G; Auricchio, A

Progress and prospects: gene therapy for genetic diseases with helper-dependent adenoviral vectors

进展与展望:利用辅助依赖型腺病毒载体进行遗传疾病基因治疗

Brunetti-Pierri, N; Ng, P