Genome editing using Staphylococcus aureus Cas9 in a canine model of glycogen storage disease Ia
使用金黄色葡萄球菌 Cas9 在犬糖原累积病 Ia 模型中进行基因组编辑
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:
doi:10.1016/j.omtm.2023.03.001
Benjamin Arnson, Hye Ri Kang, Elizabeth D Brooks, Dorothy Gheorghiu, Ekaterina Ilich, David Courtney, Jeffrey I Everitt, Bryan R Cullen, Dwight D Koeberl