Efficient delivery of RNAi prodrugs containing reversible charge-neutralizing phosphotriester backbone modifications
含有可逆电荷中和磷酸三酯骨架修饰的 RNAi 前药的有效递送
期刊:Nature Biotechnology
影响因子:33.1
doi:10.1038/nbt.3078
Bryan R Meade, Khirud Gogoi, Alexander S Hamil, Caroline Palm-Apergi, Arjen van den Berg, Jonathan C Hagopian, Aaron D Springer, Akiko Eguchi, Apollo D Kacsinta, Connor F Dowdy, Asaf Presente, Peter Lönn, Manuel Kaulich, Naohisa Yoshioka, Edwige Gros, Xian-Shu Cui, Steven F Dowdy