Contaminating plasmid sequences and disrupted vector genomes in the liver following adeno-associated virus gene therapy
腺相关病毒基因治疗后肝脏中存在的污染质粒序列和破坏的载体基因组
期刊:Nature Medicine
影响因子:50
doi:10.1038/s41591-025-04073-z
Buddle, Sarah; Brown, Li-An K; Morfopoulou, Sofia; Torres Montaguth, Oscar Enrique; Scoto, Mariacristina; Herder, Vanessa; Dhawan, Anil; Brown, Julianne R; Atkinson, Laura; Kopec, Angelika; Davis, Dee; Storey, Nathaniel; Campos, Luis; Sebire, Neil; Macpherson, Hannah; Lee, Jasmaine; Orton, Richard; Baranello, Giovanni; Asamaphan, Patawee; Ilia, Georgios; Karda, Rajvinder; Belfield, Holly; Counsell, John; Waddington, Simon N; Thomson, Emma C; Muntoni, Francesco; Breuer, Judith