Eltrombopag in combination with immunosuppressive therapy in pediatric severe aplastic anemia: phase 2 ESCALATE trial
艾曲波帕联合免疫抑制疗法治疗儿童重型再生障碍性贫血:ESCALATE II期试验
期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2024015102
Shimamura, Akiko; Maschan, Alexey; Bennett, Carolyn; Samarasinghe, Sujith; Farrar, Jason E; Li, Chi-Kong; Sirachainan, Nongnuch; Pongtanakul, Bunchoo; Komvilaisak, Patcharee; Zubarovskaya, Ludmila; Rothman, Jennifer A; Walkovich, Kelly; Nakano, Taizo A; Bertuch, Alison A; Ferrao, Anabela; Bhat, Rukhmi; Hanna, Rabi; Overholt, Kathleen; Boklan, Jessica; Wong, Tze Fang; Wang, Qinxia; Urban, Patrick; Strahm, Brigitte; Wang, Winfred; Vlachos, Adrianna; Williams, David A