Crossing the finish line towards a disease-modifying treatment for Angelman syndrome
距离研发出安格曼综合征的疾病改善疗法又近了一步
期刊:Journal of Neurodevelopmental Disorders
影响因子:4
doi:10.1186/s11689-026-09681-5
Judson, Matthew C; de Almeida, Luis Pereira; Burdine, Rebecca D; Chamberlain, Stormy J; Deverman, Benjamin E; Distel, Ben; Ehlers, Michael D; Jalazo, Elizabeth; Kushner, Steven A; Nespeca, Mark; Sanders, Stephan J; Scheffner, Martin; Yi, Jason J; Zylka, Mark J; Elgersma, Ype; Philpot, Benjamin D