Phase 2b program with sonlicromanol in patients with mitochondrial disease due to m.3243A>G mutation
针对因 m.3243A>G 突变引起的线粒体疾病患者,开展了 sonlicromanol 的 IIb 期临床试验项目。
期刊:Brain
影响因子:11.7
doi:10.1093/brain/awae277
Smeitink, Jan; van Es, Just; Bosman, Brigitte; Janssen, Mirian C H; Klopstock, Thomas; Gorman, Grainne; Vissing, John; Ruiterkamp, Gerrit; Edgar, Chris J; Abbink, Evertine J; van Maanen, Rob; Pogoryelova, Oksana; Stendel, Claudia; Bischoff, Almut; Karin, Ivan; Munshi, Mahtab; Kümmel, Anne; Burgert, Lydia; Verhaak, Christianne; Renkema, Herma