Gene therapy for Lafora disease in the Epm2a(-/-) mouse model.
在 Epm2a(-/-) 小鼠模型中对 Lafora 病进行基因治疗
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.05.032
Zafra-Puerta Luis, Iglesias-Cabeza Nerea, Burgos Daniel F, Sciaccaluga Miriam, González-Fernández Juan, Bellingacci Laura, Canonichesi Jacopo, Sánchez-MartÃn Gema, Costa Cinzia, Sánchez Marina P, Serratosa José M