日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Spinal Muscular Atrophy Update in Best Practices: Recommendations for Treatment Considerations

脊髓性肌萎缩症最佳实践更新:治疗注意事项建议

Schroth, Mary K; Deans, Jennifer; Bharucha Goebel, Diana X; Burnette, W Bryan; Darras, Basil T; Elsheikh, Bakri H; Felker, Marcia V; Klein, Andrea; Krueger, Jena; Proud, Crystal M; Veerapandiyan, Aravindhan; Graham, Robert J

Physical Activity Correlates With Skeletal Muscle MRI Findings in Individuals With Duchenne Muscular Dystrophy

身体活动与杜氏肌营养不良症患者的骨骼肌MRI检查结果相关

Tamaroff, Jaclyn; Joy, Nicholas; Damon, Bruce; Markham, Larry W; Donnelly, Thomas; Su, Karry; Buchowski, Maciej S; Crum, Kimberly; Slaughter, James C; Xu, Meng; Burnette, W Bryan; Soslow, Jonathan

Physical activity and cardiac function in patients with Duchenne muscular dystrophy

杜氏肌营养不良症患者的身体活动和心脏功能

Killian, Mary; Tamaroff, Jaclyn; Su, Karry; Crum, Kimberly; George-Durrett, Kristen; Markham, Larry W; Buchowski, Maciej; Donnelly, Thomas; Burnette, W Bryan; Soslow, Jonathan H

Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial

不同皮质类固醇剂量方案对杜氏肌营养不良症男孩临床疗效的影响:一项随机临床试验

Guglieri, Michela; Bushby, Kate; McDermott, Michael P; Hart, Kimberly A; Tawil, Rabi; Martens, William B; Herr, Barbara E; McColl, Elaine; Speed, Chris; Wilkinson, Jennifer; Kirschner, Janbernd; King, Wendy M; Eagle, Michelle; Brown, Mary W; Willis, Tracey; Griggs, Robert C; Straub, Volker; van Ruiten, Henriette; Childs, Anne-Marie; Ciafaloni, Emma; Shieh, Perry B; Spinty, Stefan; Maggi, Lorenzo; Baranello, Giovanni; Butterfield, Russell J; Horrocks, I A; Roper, Helen; Alhaswani, Zoya; Flanigan, Kevin M; Kuntz, Nancy L; Manzur, Adnan; Darras, Basil T; Kang, Peter B; Morrison, Leslie; Krzesniak-Swinarska, Monika; Mah, Jean K; Mongini, Tiziana E; Ricci, Federica; von der Hagen, Maja; Finkel, Richard S; O'Reardon, Kathleen; Wicklund, Matthew; Kumar, Ashutosh; McDonald, Craig M; Han, Jay J; Joyce, Nanette; Henricson, Erik K; Schara-Schmidt, Ulrike; Gangfuss, Andrea; Wilichowski, Ekkehard; Barohn, Richard J; Statland, Jeffrey M; Campbell, Craig; Vita, Giuseppe; Vita, Gian Luca; Howard, James F Jr; Hughes, Imelda; McMillan, Hugh J; Pegoraro, Elena; Bello, Luca; Burnette, W Bryan; Thangarajh, Mathula; Chang, Taeun

Leveraging cardiac magnetic resonance imaging to assess skeletal muscle progression in Duchenne muscular dystrophy

利用心脏磁共振成像评估杜氏肌营养不良症患者的骨骼肌进展

Kaslow, Jacob A; Sokolow, Andrew G; Donnelly, Thomas; Buchowski, Maciej S; Damon, Bruce M; Markham, Larry W; Burnette, W Bryan; Soslow, Jonathan H

Assessing Physical Activity Using Accelerometers in Youth with Duchenne Muscular Dystrophy

利用加速度计评估杜氏肌营养不良症青少年的身体活动

Arteaga, David; Donnelly, Thomas; Crum, Kimberly; Markham, Larry; Killian, Mary; Burnette, W Bryan; Soslow, Jonathan; Buchowski, Maciej S

Creation of a novel algorithm to identify patients with Becker and Duchenne muscular dystrophy within an administrative database and application of the algorithm to assess cardiovascular morbidity

创建一种新的算法,用于在行政数据库中识别贝克尔型和杜氏肌营养不良症患者,并将该算法应用于评估心血管疾病发病率。

Soslow, Jonathan H; Hall, Matthew; Burnette, W Bryan; Hor, Kan; Chisolm, Joanne; Spurney, Christopher; Godown, Justin; Xu, Meng; Slaughter, James C; Markham, Larry W

Recruitment & retention program for the NeuroNEXT SMA Biomarker Study: Super Babies for SMA!

NeuroNEXT SMA 生物标志物研究的招募和留任计划:SMA 超级宝宝!

Bartlett, Amy; Kolb, Stephen J; Kingsley, Allison; Swoboda, Kathryn J; Reyna, Sandra P; Sakonju, Ai; Darras, Basil T; Shell, Richard; Kuntz, Nancy; Castro, Diana; Iannaccone, Susan T; Parsons, Julie; Connolly, Anne M; Chiriboga, Claudia A; McDonald, Craig; Burnette, W Bryan; Werner, Klaus; Thangarajh, Mathula; Shieh, Perry B; Finanger, Erika; Coffey, Christopher S; Yankey, Jon W; Cudkowicz, Merit E; McGovern, Michelle M; McNeil, D Elizabeth; Arnold, W David; Kissel, John T

Natural history of infantile-onset spinal muscular atrophy

婴儿期发病脊髓性肌萎缩症的自然史

Kolb, Stephen J; Coffey, Christopher S; Yankey, Jon W; Krosschell, Kristin; Arnold, W David; Rutkove, Seward B; Swoboda, Kathryn J; Reyna, Sandra P; Sakonju, Ai; Darras, Basil T; Shell, Richard; Kuntz, Nancy; Castro, Diana; Parsons, Julie; Connolly, Anne M; Chiriboga, Claudia A; McDonald, Craig; Burnette, W Bryan; Werner, Klaus; Thangarajh, Mathula; Shieh, Perry B; Finanger, Erika; Cudkowicz, Merit E; McGovern, Michelle M; McNeil, D Elizabeth; Finkel, Richard; Iannaccone, Susan T; Kaye, Edward; Kingsley, Allison; Renusch, Samantha R; McGovern, Vicki L; Wang, Xueqian; Zaworski, Phillip G; Prior, Thomas W; Burghes, Arthur H M; Bartlett, Amy; Kissel, John T

Increased Number of Circulating CD8/CD26 T Cells in the Blood of Duchenne Muscular Dystrophy Patients Is Associated with Augmented Binding of Adenosine Deaminase and Higher Muscular Strength Scores.

杜氏肌营养不良症患者血液中循环 CD8/CD26 T 细胞数量的增加与腺苷脱氨酶结合增强和肌肉力量评分提高有关

Soslow Jonathan H, Markham Larry W, Burnette W Bryan, Galindo Cristi L, Feoktistov Igor, Raucci Frank J Jr, Damon Bruce M, Sawyer Douglas B, Ryzhov Sergey