日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Large-scale RNA-Seq mining reveals ciclopirox olamine induces TDP-43 cryptic exons.

大规模 RNA-Seq 挖掘揭示环吡咯醇胺诱导 TDP-43 隐蔽外显子

Sinha Irika R, Sandal Parker S, Spence Holly, Burns Grace D, Mallika Aswathy Peethambaran, Abbasinejad Fatemeh, Irwin Katherine E, Cruz Anna Lourdes F, Wang Vania, Marx Shaelyn R, Rodríguez Josué Llamas, Langmead Ben, Gregory Jenna M, Wong Philip C, Ling Jonathan P

Broad brain biodistribution conferred by an AAV to restore TDP-43 function mitigates Frontotemporal Demenia-like deficits

通过腺相关病毒(AAV)实现广泛的脑生物分布,从而恢复TDP-43功能,减轻额颞叶痴呆样症状。

Cao, Tianyu; Thapa, Rashmi; Liu, Rongsong; Mallika, Aswathy Peethambaran; Baghel, Meghraj Singh; Wei, Yijun; Sinha, Irika R; Burns, Grace D; Wen, Xinrui; Pang, Bo; Ling, Jonathan P; Lin, Da-Ting; Li, Yun; Wong, Philip C