Cas9-induced single cut enables highly efficient and template-free repair of a muscular dystrophy causing founder mutation
Cas9 诱导的单次切割能够高效、无模板地修复引起创始突变的肌营养不良症
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2023.02.005
Stefanie Müthel, Andreas Marg, Busem Ignak, Janine Kieshauer, Helena Escobar, Christian Stadelmann, Simone Spuler
