Antisense Oligonucleotide Therapy Targeted Against ATXN3 Improves Potassium Channel-Mediated Purkinje Neuron Dysfunction in Spinocerebellar Ataxia Type 3
针对ATXN3的反义寡核苷酸疗法可改善脊髓小脑性共济失调3型中钾通道介导的浦肯野神经元功能障碍
期刊:Cerebellum
影响因子:2.4
doi:10.1007/s12311-020-01179-7
Bushart, David D; Zalon, Annie J; Zhang, Hongjiu; Morrison, Logan M; Guan, Yuanfang; Paulson, Henry L; Shakkottai, Vikram G; McLoughlin, Hayley S