Novel factor VIII variants with a modified furin cleavage site improve the efficacy of gene therapy for hemophilia A
具有改良弗林蛋白酶切割位点的新型 VIII 因子变体可提高 A 型血友病基因治疗的疗效
期刊:Journal of Thrombosis and Haemostasis
影响因子:5.5
doi:10.1111/jth.13543
G N Nguyen, L A George, J I Siner, R J Davidson, C B Zander, X L Zheng, V R Arruda, R M Camire, D E Sabatino