Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome
慢病毒造血干/祖细胞基因治疗Wiskott-Aldrich综合征的长期安全性和有效性
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-021-01641-x
A Magnani #, M Semeraro #, F Adam, C Booth, L Dupré, E C Morris, A Gabrion, C Roudaut, D Borgel, A Toubert, E Clave, C Abdo, G Gorochov, R Petermann, M Guiot, M Miyara, D Moshous, E Magrin, A Denis, F Suarez, C Lagresle, A M Roche, J Everett, A Trinquand, M Guisset, J Xu Bayford, S Hacein-Bey-Abina,