Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy
基因编辑技术在杜氏肌营养不良症犬模型中恢复了肌营养不良蛋白的表达
期刊:Science
影响因子:45.8
doi:10.1126/science.aau1549
Amoasii, Leonela; Hildyard, John C W; Li, Hui; Sanchez-Ortiz, Efrain; Mireault, Alex; Caballero, Daniel; Harron, Rachel; Stathopoulou, Thaleia-Rengina; Massey, Claire; Shelton, John M; Bassel-Duby, Rhonda; Piercy, Richard J; Olson, Eric N