Treatment of canine hemophilia A via intraosseous delivery of a platelet-specific factor VIII-lentiviral vector
通过骨内注射血小板特异性因子VIII慢病毒载体治疗犬血友病A
期刊:
影响因子:
doi:10.1016/j.bvth.2025.100119
Rementer, Cameron W; Li, Chong; Nichols, Timothy C; Cai, Xiaohe; Joo, Julia; Wang, Xuefeng; Kloos, Mark; George, Nneka; Chao, Ting-Yen; Xu, Yuanyi; Poncz, Mortimer; Ochs, Hans D; Rawlings, David J; Miao, Carol H