Trans-spliced Cas9 allows cleavage of HBB and CCR5 genes in human cells using compact expression cassettes
转接的 Cas9 允许使用紧凑的表达盒在人类细胞中裂解 HBB 和 CCR5 基因
期刊:Scientific Reports
影响因子:3.8
doi:10.1038/srep10777
Eli J Fine, Caleb M Appleton, Douglas E White, Matthew T Brown, Harshavardhan Deshmukh, Melissa L Kemp, Gang Bao