Effect of VX-770 in persons with cystic fibrosis and the G551D-CFTR mutation
VX-770 对囊性纤维化合并 G551D-CFTR 突变患者的影响
期刊:New England Journal of Medicine
影响因子:78.5
doi:10.1056/NEJMoa0909825
Accurso, Frank J; Rowe, Steven M; Clancy, J P; Boyle, Michael P; Dunitz, Jordan M; Durie, Peter R; Sagel, Scott D; Hornick, Douglas B; Konstan, Michael W; Donaldson, Scott H; Moss, Richard B; Pilewski, Joseph M; Rubenstein, Ronald C; Uluer, Ahmet Z; Aitken, Moira L; Freedman, Steven D; Rose, Lynn M; Mayer-Hamblett, Nicole; Dong, Qunming; Zha, Jiuhong; Stone, Anne J; Olson, Eric R; Ordoñez, Claudia L; Campbell, Preston W; Ashlock, Melissa A; Ramsey, Bonnie W