日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Cross-species validation of a human age-related hearing loss candidate KLHDC7B as essential for mammalian hearing

跨物种验证人类年龄相关性听力损失候选基因KLHDC7B对哺乳动物听力至关重要

Kaufman, Alexandra M; Silver, Benjamin; Donnianni, Roberto A; Aguilar, Carlos; Niu, Lingzi; Johnson, Daniel; Bullen, Anwen; Corona, Alma; van Soldt, Benjamin J; Vora, Nilay; Batista, Gervasio; Cortes-Burgos, Luz; Copeland, Jacqueline; Fallah, Elika; Zhang, Norman; Lehmkuhl, Marina; Cancelarich, Sarah; Campos, Kara; Di Battista Miani, Daniela; Mumphrey, Jaylen; Croll, Susan D; Walls, Johnathon R; Germino, Mary; Bowl, Michael R; Drummond, Meghan C; Dawson, Sally J

Functional, sustained recovery of hearing in Otoferlin-deficient mice using DB-OTO, a hair-cell-specific AAV-based gene therapy.

使用 DB-OTO(一种基于 AAV 的毛细胞特异性基因疗法)使 Otoferlin 缺陷小鼠的听力得到功能性、持续性恢复。

Chung Yoojin, Koehler Seth D, Cancelarich Sarah, Gibson Tyler M, Pregernig Gabriela, Becker Lars, Artinian Quynh-Anh, Goodliffe Joseph W, Pan Ning, Quigley Tera M, Senapati Arun, Slade Peter G, Smith Lillian M, So Kathy S, Zhang Xichun, Corrales C Eduardo, Weber Peter, Macdonald Lynn E, Zambrowicz Brian, Economides Aris N, Kyratsous Christos A, Burns Joseph C, Palermo Adam T, Sabin Leah R, Lee John, Valayannopoulos Vassili, Whitton Jonathon P, Drummond Meghan C

Recovery kinetics of dual AAV-mediated human otoferlin expression

双 AAV 介导的人类耳畸蛋白表达的恢复动力学

Jonathan B Sellon, Kathy S So, Andrew D'Arcangelo, Sarah Cancelarich, Meghan C Drummond, Peter G Slade, Ning Pan, Tyler M Gibson, Tian Yang, Joseph C Burns, Adam T Palermo, Lars Becker

Accelerating the Discovery and Design of Antimicrobial Peptides with Artificial Intelligence

利用人工智能加速抗菌肽的发现和设计

Aguilera-Puga, Mariana D C; Cancelarich, Natalia L; Marani, Mariela M; de la Fuente-Nunez, Cesar; Plisson, Fabien

Tissue-specific activation of gene expression by the Synergistic Activation Mediator (SAM) CRISPRa system in mice

协同激活介质 (SAM) CRISPRa 系统在小鼠中实现组织特异性基因表达激活

Charleen Hunt #, Suzanne A Hartford #, Derek White, Evangelos Pefanis, Timothy Hanna, Clarissa Herman, Jarrell Wiley, Heather Brown, Qi Su, Yurong Xin, Dennis Voronin, Hien Nguyen, Judith Altarejos, Keith Crosby, Jeffery Haines, Sarah Cancelarich, Meghan Drummond, Sven Moller-Tank, Ryan Malpass, Jac

Identification of New Ocellatin Antimicrobial Peptides by cDNA Precursor Cloning in the Frame of This Family of Intriguing Peptides

利用cDNA前体克隆技术鉴定该家族新型Ocellatin抗菌肽

Marani, Mariela M; Aguilar, Silvana; Cuzziol Boccioni, Ana P; Cancelarich, Natalia L; Basso, Néstor G; Albericio, Fernando