Nanoparticles that deliver triplex-forming peptide nucleic acid molecules correct F508del CFTR in airway epithelium
递送三链体形成肽核酸分子的纳米颗粒可纠正气道上皮细胞中的F508del CFTR突变。
期刊:Nature Communications
影响因子:15.7
doi:10.1038/ncomms7952
McNeer, Nicole Ali; Anandalingam, Kavitha; Fields, Rachel J; Caputo, Christina; Kopic, Sascha; Gupta, Anisha; Quijano, Elias; Polikoff, Lee; Kong, Yong; Bahal, Raman; Geibel, John P; Glazer, Peter M; Saltzman, W Mark; Egan, Marie E