日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Efficacy and safety of marstacimab prophylaxis in hemophilia A/B with inhibitors: results from the phase 3 BASIS trial

marstacimab预防治疗A/B型血友病伴抑制剂的疗效和安全性:来自3期BASIS试验的结果

Matino, Davide; Acharya, Suchitra S; Taylor, Carrie Turich; Sun, Pengling; Agathon, Delphine; Raje, Sangeeta; Gould, Travis; Palladino, Andrew; Mahlangu, Johnny; Lissitchkov, Toshko; Todorova, Mariya; Chan, Anthony; Carcao, Manuel; Sun, Jing; Yang, Renchi; Wu, Runhui; Jin, Chenghao; Zeng, Xiaojing; Boban, Ana; Bilic, Ernest; Frenzel, Laurent; Fung Chan, Godfrey Chi; Kong Li, Chi; Apte, Shashikant; Choraria, Nirmalkumar; Chistolini, Antonio; Marchesini, Emanuela; Peyvandi, Flora; Fujii, Teruhisa; Matsushita, Tadashi; Kaneda, Makoto; Lyu, Chuhl Joo; Park, Young Shil; Kim, SungEun; Martinez, Laura Villarreal; Adrian, Javier Morales; Wali, Yasser; Al Khabori, Murtadha; Kurtov, Igor; Alzahrani, Hazzaa; Zaher, Galila; Micic, Dragan; Miljic, Predrag; Kostic, Gordana; Vucic, Miodrag; Djurdjevic, Predrag; Hidalgo, Olga Benitez; Porras, Jose Gonzalez; Jiménez-Yuste, Víctor; Calvo Villas, Jose Manuel; Lopez Fernandez, Maria Fernanda; Albayrak, Canan; Okan, Vahap; Balkan, Can; Sahin, Fahri; Antmen, Ali; Unal, Ekrem; Visweshwar, Nathan; Sharathkumar, Anjali; Kruse-Jarres, Rebecca

Cerebral sinus venous thrombosis in a child with Québec platelet disorder with high-resolution intracellular localization of urokinase in platelets

一名患有魁北克血小板疾病的儿童出现脑静脉窦血栓形成,并进行了血小板内尿激酶的高分辨率细胞内定位研究

Zabeida, Alexandra; Mathews, Natalie; Bouskill, Vanessa; Vincelli, Jennifer; Williams, Suzan; Pluthero, Fred G; Carcao, Manuel; Kahr, Walter H A

Factor XIII deficiency due to compound heterozygosity for 2 F13A1 variants

由于两种 F13A1 变异体的复合杂合性导致的 XIII 因子缺乏症

Odame, Jodie; Malcolmson, Caroline; Wakefield, Cindy; Bourque, Tammy; Lillicrap, David; Rawley, Orla; Bowman, Mackenzie; Carcao, Manuel; Bouskill, Vanessa

Large deletions in the F8 gene predict immune tolerance induction failure in people with severe hemophilia A

F8基因的大片段缺失预示着重度A型血友病患者免疫耐受诱导失败。

Oomen, Ilja; Abdi, Amal; Broer, Linda; Camelo, Ricardo M; Callado, Fábia M R A; Carvalho, Luany E M; Calcaterra, Ilenia L; Carcao, Manuel; Castaman, Giancarlo; Eikenboom, Jeroen C J; Fischer, Kathelijn; Franco, Vivian K B; Geissler, Judy; Kuijpers, Taco W; Leebeek, Frank W G; Lillicrap, David; Lorenzato, Cláudia S; Mancuso, Maria Elisa; Matino, Davide; Di Minno, Matteo N D; Mo, Aomei; Mohseny, Alex B; Nagelkerke, Sietse Q; Oldenburg, Johannes; Rezende, Suely Meireles; Rivard, Georges-Etienne; Rydz, Natalia; Schols, Saskia E M; Tanck, Michael W T; Voorberg, Jan; Fijnvandraat, Karin; Gouw, Samantha C

Safety and Use of Eptacog Beta 225 µg/kg in Patients With Haemophilia A or B With Inhibitors

Eptacog Beta 225 µg/kg 在伴有抑制物的 A 型或 B 型血友病患者中的安全性和使用

Carcao, Manuel; Hermans, Cédric; Giermasz, Adam; Kessler, Craig; Miesbach, Wolfgang; Quon, Doris; Windyga, Jerzy; Mahlangu, Johnny

Bleed treatment with eptacog beta (rFVIIa) results in a low incidence of rebleeding in adult and adolescent patients with haemophilia A or B with inhibitors

使用重组人凝血因子VIIa (rFVIIa) 治疗出血,可降低伴有抑制因子的A型或B型血友病成人和青少年患者的再出血发生率。

Dunn, Amy; Dargaud, Yesim; Abajas, Yasmina; Carcao, Manuel; Castaman, Giancarlo; Giermasz, Adam; Hermans, Cédric; Jiménez-Yuste, Victor; Lewandowska, Magdalena; Mahlangu, Johnny; Meeks, Shannon; Miesbach, Wolfgang; Recht, Michael; Salinas, Vanessa; Chrisentery-Singleton, Tammuella; Bonzo, Daniel; Mitchell, Ian S; Wilkinson, Thomas A; Young, Guy

Comparison of Magnetic Resonance Imaging Scales for Assessment of Interval Changes of Arthropathy in Boys with Severe Hemophilia

比较磁共振成像量表在评估重度血友病男孩关节病变间隔变化中的应用

Zhang, Ningning; Carcao, Manuel; Ignas, Danial M; Feldman, Brian M; Hilliard, Pamela; Moineddin, Rahim; Stain, Ann Marie; Babyn, Paul; Blanchette, Victor S; Doria, Andrea S

Safe Endoscopic Treatment for a Bleeding Infant With Multifocal Lymphangioendotheliomatosis and Thrombocytopenia (MLT)

安全内镜治疗伴有多灶性淋巴管内皮瘤病和血小板减少症(MLT)的出血婴儿

Steg Saban, Or; Pope, Elena; Chavhan, Govind B; Carcao, Manuel; Talarico, Susanna; Ling, Simon C

Treatment of severe bleeds with eptacog beta in hemophilia A or B with inhibitors: a post hoc analysis of the PERSEPT 1 and 2 trials

使用依普塔可格β治疗伴有抑制因子的A型或B型血友病患者的严重出血:PERSEPT 1和2试验的事后分析

Young, Guy; Mahlangu, Johnny; Boggio, Lisa N; Carcao, Manuel; Dargaud, Yesim; Escobar, Miguel; Giermasz, Adam; Hermans, Cédric; Kuriakose, Philip; Miesbach, Wolfgang; Nance, Danielle; Rafique, Amina; Sidonio, Robert F Jr; Vilchevska, Kateryna V; Wang, Michael; Pipe, Steven W

A post hoc analysis of previously untreated patients with severe hemophilia A who developed inhibitors in the PUPs A-LONG trial

对 PUPs A-LONG 试验中既往未接受治疗的重度血友病 A 患者进行事后分析,这些患者在试验中产生了抑制剂。

Carcao, Manuel; Schiavulli, Michele; Kulkarni, Roshni; Rendo, Pablo; Foster, Meredith; Santagostino, Elena; Casiano, Sandra; Königs, Christoph