Early biochemical effects of velmanase alfa in a 7-month-old infant with alpha-mannosidosis
velmanase alfa 对 7 个月大患 α-甘露糖苷贮积症的婴儿的早期生化影响
期刊:JIMD Reports
影响因子:
doi:10.1002/jmd2.12144
Lucia Santoro, Lucia Zampini, Lucia Padella, Chiara Monachesi, Stefania Zampieri, Andrea Dardis, Rosanna Cordiali, Tiziana Galeazzi, Carlo Catassi