Downregulation of rhodopsin is an effective therapeutic strategy in ameliorating peripherin-2-associated inherited retinal disorders
视紫红质下调是改善周围蛋白-2相关遗传性视网膜疾病的有效治疗策略
期刊:Nature Communications
影响因子:14.7
doi:10.1038/s41467-024-48846-5
Christian T Rutan Woods, Mustafa S Makia, Tylor R Lewis, Ryan Crane, Stephanie Zeibak, Paul Yu, Mashal Kakakhel, Carson M Castillo, Vadim Y Arshavsky, Muna I Naash, Muayyad R Al-Ubaidi