Update on the safety and efficacy of retroviral gene therapy for immunodeficiency due to adenosine deaminase deficiency
关于逆转录病毒基因疗法治疗腺苷脱氨酶缺乏症所致免疫缺陷的安全性和有效性的最新进展
期刊:Blood
影响因子:23.1
doi:10.1182/blood-2016-01-688226
Cicalese, Maria Pia; Ferrua, Francesca; Castagnaro, Laura; Pajno, Roberta; Barzaghi, Federica; Giannelli, Stefania; Dionisio, Francesca; Brigida, Immacolata; Bonopane, Marco; Casiraghi, Miriam; Tabucchi, Antonella; Carlucci, Filippo; Grunebaum, Eyal; Adeli, Mehdi; Bredius, Robbert G; Puck, Jennifer M; Stepensky, Polina; Tezcan, Ilhan; Rolfe, Katie; De Boever, Erika; Reinhardt, Rickey R; Appleby, Jonathan; Ciceri, Fabio; Roncarolo, Maria Grazia; Aiuti, Alessandro
