日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

TNFα signaling restores steady-state hematopoiesis in a TNFαKO mouse model of anemia of inflammation

在炎症性贫血的TNFαKO小鼠模型中,TNFα信号通路可恢复稳态造血功能。

Guerra, Amaliris; Lo Presti, Vania; Chen, Ding-Wen; Martins, Ana Catarina; Rivera, Ariel; Hamilton, Nolan; Sharma, Pankja; Ginzburg, Yelena Z; Castruccio Castracani, Carlo; Casu, Carla; Gupta, Ritama; Gozzelino, Raffaella; Behrens, Edward M; Bennett, Laura F; Paulson, Robert F; Kurre, Peter; Rivella, Stefano

An erythroid-specific lentiviral vector improves anemia and iron metabolism in a new model of XLSA

一种红细胞特异性慢病毒载体可改善XLSA新模型中的贫血和铁代谢。

Castruccio Castracani, Carlo; Breda, Laura; Papp, Tyler E; Guerra, Amaliris; Radaelli, Enrico; Assenmacher, Charles-Antoine; Finesso, Giovanni; Mui, Barbara L; Tam, Ying K; Fontana, Simona; Riganti, Chiara; Fiorito, Veronica; Petrillo, Sara; Tolosano, Emanuela; Parhiz, Hamideh; Rivella, Stefano

Effective gene therapy for metachromatic leukodystrophy achieved with minimal lentiviral genomic integrations

利用最小的慢病毒基因组整合实现对异染性脑白质营养不良的有效基因治疗

Lucas Tricoli ,Sunetra Sase ,Julia L Hacker ,Vi Pham ,Maxwell Chappell ,Laura Breda ,Stephanie N Hurwitz ,Naoto Tanaka ,Carlo Castruccio Castracani ,Amaliris Guerra ,Zhongqi Hou ,Lars Schlotawa ,Karthikeyan Radhakrishnan ,Matthew Hogenauer ,Aoife Roche ,John Everett ,Frederic Bushman ,Peter Kurre ,Rebecca Ahrens-Nicklas ,Laura A Adang ,Adeline L Vanderver ,Stefano Rivella

Recycle and reuse: an ethological perspective for citizen science data on Lucanus cervus (Coleoptera: Lucanidae)

回收再利用:基于公民科学数据的鹿角锹甲(鞘翅目:锹甲科)行为学视角

Gisondi, Silvia; Spotti, Fiorenza Augusta; Lenzi, Alice; Grasso, Donato Antonio; Campanaro, Alessandro; Castracani, Cristina

Use of HSC-targeted LNP to generate a mouse model of lethal α-thalassemia and treatment via lentiviral gene therapy

利用靶向造血干细胞的脂质纳米颗粒构建致死性α-地中海贫血小鼠模型,并通过慢病毒基因治疗进行治疗。

Chappell, Maxwell E; Breda, Laura; Tricoli, Lucas; Guerra, Amaliris; Jarocha, Danuta; Castruccio Castracani, Carlo; Papp, Tyler E; Tanaka, Naoto; Hamilton, Nolan; Triebwasser, Michael P; Ghiaccio, Valentina; Fedorky, Megan T; Gollomp, Kandace L; Bochenek, Veronica; Roche, Aoife M; Everett, John K; Cook, Emma J; Bushman, Frederic D; Teawtrakul, Nattiya; Glentis, Stavros; Kattamis, Antonis; Mui, Barbara L; Tam, Ying K; Weissman, Drew; Abdulmalik, Osheiza; Parhiz, Hamideh; Rivella, Stefano

Hematopoietic stem cell gene therapy improves outcomes in a clinically relevant mouse model of multiple sulfatase deficiency

造血干细胞基因疗法改善了具有临床意义的多发性硫酸酯酶缺乏症小鼠模型的预后。

Vi Pham ,Lucas Tricoli ,Xinying Hong ,Parith Wongkittichote ,Carlo Castruccio Castracani ,Amaliris Guerra ,Lars Schlotawa ,Laura A Adang ,Amanda Kuhs ,Margaret M Cassidy ,Owen Kane ,Emily Tsai ,Maximiliano Presa ,Cathleen Lutz ,Stefano B Rivella ,Rebecca C Ahrens-Nicklas

Correction: Sigma-1 and Sigma-2 receptor ligands induce apoptosis and autophagy but have opposite effect on cell proliferation in uveal melanoma

更正:Sigma-1 和 Sigma-2 受体配体可诱导细胞凋亡和自噬,但对葡萄膜黑色素瘤细胞增殖的影响相反。

Longhitano, Lucia; Castracani, Carlo Castruccio; Tibullo, Daniele; Avola, Roberto; Viola, Maria; Russo, Giuliano; Prezzavento, Orazio; Marrazzo, Agostino; Amata, Emanuele; Reibaldi, Michele; Longo, Antonio; Russo, Andrea; Parrinello, Nunziatina Laura; Volti, Giovanni Li

Do It by Yourself: Larval Locomotion in the Black Soldier Fly Hermetia illucens, with a Novel "Self-Harvesting" Method to Separate Prepupae

自己动手:黑水虻幼虫的运动,以及一种分离预蛹的新型“自收获”方法

Giannetti, Daniele; Schifani, Enrico; Reggiani, Roberto; Mazzoni, Emanuele; Reguzzi, Maria Cristina; Castracani, Cristina; Spotti, Fiorenza A; Giardina, Beatrice; Mori, Alessandra; Grasso, Donato A

S101: COMBINATION OF A LUSPATERCEPT-LIKE DRUG (RAP-GRL) AND TMPRSS6-ASO IS SUPERIOR TO EITHER DRUG ALONE FOR CORRECTING β-THALASSEMIA

S101:LUSPATERCEPT 样药物 (RAP-GRL) 与 TMPRSS6-ASO 联合用药在纠正 β-地中海贫血方面优于单独使用任何一种药物

Trojani, Alessandra; Montillo, Marco; Nichelatti, Michele; Tedeschi, Alessandra; Colombo, Chiara; Veronese, Silvio; Mura, Maria Angela; Ricci, Francesca; Scarpati, Barbara; Colosimo, Anna; Lodola, Milena; Morra, Enrica; Agrippa, OA; Summers, KZ; Anie, KA; Telfer, P; Lugthart, S; De La Fuente, A; Peñalver, F J; Herrera, P; Cordoba, R; Martinez Chamorro, C; Olave, M T; Jarque, I; Navarro, M B; Estévez, M; Masarova, L; Bose, P; Pemmaraju, N; Chifotides, H; Zhou, L; Estrov, Z; Kantarjian, H; Verstovsek, S; Sgherza, N; Curci, P; Rizzi, R; Roccotelli, D; Croce, M; Avantaggiato, M; Ruga, L; Vitucci, A; Palma, A; Di Gennaro, D; Musto, P; Sgherza, N; Rizzi, R; Curci, P; Roccotelli, D; Croce, M; Avantaggiato, M; Ruga, L; Musto, P; Guerra, A; Demsko, P; Sinha, S; McVeigh, P; Castruccio Castracani, C; Breda, L; Casu, C; Rivella, S

Nutraceuticals in the Prevention of Viral Infections, including COVID-19, among the Pediatric Population: A Review of the Literature

营养保健品在预防儿童病毒感染(包括 COVID-19)中的作用:文献综述

Parisi, Giuseppe Fabio; Carota, Giuseppe; Castruccio Castracani, Carlo; Spampinato, Mariarita; Manti, Sara; Papale, Maria; Di Rosa, Michelino; Barbagallo, Ignazio; Leonardi, Salvatore