日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Development of an AAV-based gene therapy for the ocular phenotype of Friedreich's ataxia.

开发基于 AAV 的基因疗法治疗弗里德赖希共济失调的眼部表型。

Tang Heyu, Gupte Siddhant, Xu Emily, Calabro Kaitlyn R, Friend Hannah, Crosson Sean M, Fajardo Diego, Kostamo Zachary, Zhang Hangning, Peterson James J, Lin Fangyu, Kozmik Zbynek, Lutz Cathleen M, Boye Sanford L, Boye Shannon E

Beyond wingtips: backbone alkylation affects the orientation of N-heterocyclic carbenes on gold nanoparticles

除了翼尖之外:骨架烷基化影响金纳米粒子上N-杂环卡宾的取向

Nezamzadeh, Ahmadreza; Chowdhury, Shayanta; Hu, Gaohe; Dominique, Nathaniel L; Desroche, Emmett; Hossain, Sakiat; Aloisio, Mark D; Furlan, Michael; Groome, Ryan R K; Boire, Kayla; McLean, Alastair B; Jensen, Lasse; Camden, Jon P; Crudden, Cathleen M

Combined electrodeposition and electropolymerization method to produce surface-bound polystyrenyl NHC thin films

采用电沉积和电聚合相结合的方法制备表面结合的聚苯乙烯NHC薄膜

Bosso, Jessica L; Lomax, Justin T; Garg, Garima; Shiu, Wai-Tung; Bentley, Jordan N; Turnbull, Matthew J; Snowdon, Monika R; Noël, James J; Crudden, Cathleen M; Gilroy, Joe B; Ragogna, Paul J

Simon says "stay in touch": Reachability moderates the effect of irrelevant spatial congruence

西蒙说“保持联系”:可达性会缓和无关空间一致性的影响。

Paavola, Michael L; Mordkoff, J Toby; Moore, Cathleen M

Saccades to spatially extended objects: The roles of observer goals and part-structure cues in determining within-object landing position

扫视到空间扩展物体:观察者目标和部分结构线索在决定物体内部落点位置中的作用

Hollingworth, Andrew; Moore, Cathleen M

Mechanistic machine learning enables interpretable and generalizable prediction of prime editing outcomes

机制机器学习能够对主要编辑结果进行可解释且可推广的预测。

Hsu, Alvin; Chen, Peter J; Li, Angus H; Hemez, Colin F; Gao, Xin D; Terrey, Markus; Nelson, Charlie; Selvam, Vijay; Cristian, Ana; McElroy, Amber N; Steinbeck, Benjamin J; Mahadeshwar, Gandhar K; Pandey, Smriti; Barsdale, Zachary; Chen, Paul Z; Sousa, Alexander A; Sakai, Holt A; Silverstein, Rachel A; Morad, Ilias; Krueger, Ryan K; Shen, Max W; Kleinstiver, Benjamin P; Lutz, Cathleen M; Tolar, Jakub; Blazar, Bruce R; Osborn, Mark J; Liu, David R

In vivo prime editing rescues alternating hemiplegia of childhood in mice

体内基因编辑可挽救小鼠儿童交替性偏瘫

Alexander A Sousa,Markus Terrey,Holt A Sakai,Christine Q Simmons,Elena Arystarkhova,Natalia S Morsci,Laura C Anderson,Jun Xie,Fabian Suri-Payer,Linda C Laux,Emmanuel Roze,Sylvie Forlani,Guangping Gao,Simon Frost,Nina Frost,Kathleen J Sweadner,Alfred L George Jr,Cathleen M Lutz,David R Liu

A comprehensive atlas of AAV tropism in the mouse

小鼠体内AAV嗜性的综合图谱

Christopher J Walkey ,Kathy J Snow ,Jote Bulcha ,Aaron R Cox ,Alexa E Martinez ,M Cecilia Ljungberg ,Denise G Lanza ,Marco De Giorgi ,Marcel A Chuecos ,Michele Alves-Bezerra ,Carlos Flores Suarez ,Sean M Hartig ,Susan G Hilsenbeck ,Chih-Wei Hsu ,Ethan Saville ,Yaned Gaitan ,Jeff Duryea Jr ,Seth Hannigan ,Mary E Dickinson ,Oleg Mirochnitchenko ,Dan Wang ,Cathleen M Lutz ,Jason D Heaney ,Guangping Gao ,Stephen A Murray ,William R Lagor

Synaptic dysregulation in a mouse model of GRIN2D developmental and epileptic encephalopathy

GRIN2D发育和癫痫性脑病小鼠模型中的突触功能紊乱

Teoh, JiaJie; Simko, Jane; Camp, Chad R; Liu, Christine J; Wang, Wanqi; Williams, Damian J; Ma, Liang; Soundararajan, Divyalakshmi; Martin, Caryn; Taylor, Noah K; François, Ekniel; Petri, Sabrina; Kanber, Ayla; Ravichandra, Aishwarya; Pero, Maria Elena; Bartolini, Francesca; Swayne, Theresa C; Lutz, Cathleen M; Zuberi, Aamir; Rubinstein, Moran; Hausman-Kedem, Moran; Yuan, Hongjie; Gelinas, Jennifer N; Sands, Tristan T; Harper, Scott Q; Traynelis, Stephen F; Makinson, Christopher D; Frankel, Wayne N

Amyotrophic lateral sclerosis and frontotemporal dementia mutation reduces endothelial TDP-43 and causes blood-brain barrier defects

肌萎缩侧索硬化症和额颞叶痴呆的基因突变会降低内皮细胞TDP-43的水平,并导致血脑屏障缺陷。

Ashok Cheemala ,Amy L Kimble ,Emily N Burrage ,Stephen B Helming ,Jordan D Tyburski ,Nathan K Leclair ,Omar M Omar ,Aamir R Zuberi ,Melissa Murphy ,Evan R Jellison ,Bo Reese ,Xiangyou Hu ,Cathleen M Lutz ,Riqiang Yan ,Patrick A Murphy