Prime editing as a promising therapeutic strategy for junctional epidermolysis bullosa.
Prime编辑作为治疗大疱性交界性表皮松解症的一种有前途的治疗策略。
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.10.054
Hierl Markus, Bischof Johannes, Liemberger Bernadette, Kocher Thomas, Hainzl Stefan, Gruner Stefanie, Trattner Lisa, Reichl Victoria, Klausegger Alfred, Aussel Clotilde, Ammann Sandra, Raab Rebecca, Andrieux Geoffroy, Wolf Martin, Hochmann Sarah, Ebner Patricia, Wally Verena, Zauner Roland, Guttmann-Gruber Christina, Gratz Iris K, Hofbauer Josefina Piñón, Cathomen Toni, Strunk Dirk, Bauer Johann W, Koller Ulrich