日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

ERCC6L2 ensures repair fidelity for staggered-end DNA double-strand breaks.

ERCC6L2 确保交错末端 DNA 双链断裂的修复保真度。

Aird Eric J, Serrano-Benitez Almudena, Siegner Sebastian M, Cannavo Elda, Belotserkovskaya Rimma, Gueorguieva Nadia, Fielden John, Cullot Grégoire, Ammann Sandra, Bader Aldo S, Gupta Vipul, Andrieux Geoffroy, Raab Rebecca, Del Rey González Mónica, Cathomen Toni, Cejka Petr, Corn Jacob E, Jackson Stephen P

Base edited skin equivalents with clinical potential for ex vivo correction of recessive dystrophic epidermolysis bullosa

具有临床潜力的基础编辑皮肤等效物,可用于体外矫正隐性营养不良性大疱性表皮松解症

Bassons-Bascuñana, Alex; Duarte, Blanca; Méndez-Jiménez, Estela; Ugalde, Laura; Sanabria-Betrián, Paula; Aussel, Clotilde; Peña-Gutiérrez, Irene; Olalla-Sastre, Beatriz; Ammann, Sandra; Cathomen, Toni; Del Rio, Marcela; Río, Paula; Larcher, Fernando; López-Manzaneda, Sergio

Prime editing as a promising therapeutic strategy for junctional epidermolysis bullosa.

Prime编辑作为治疗大疱性交界性表皮松解症的一种有前途的治疗策略。

Hierl Markus, Bischof Johannes, Liemberger Bernadette, Kocher Thomas, Hainzl Stefan, Gruner Stefanie, Trattner Lisa, Reichl Victoria, Klausegger Alfred, Aussel Clotilde, Ammann Sandra, Raab Rebecca, Andrieux Geoffroy, Wolf Martin, Hochmann Sarah, Ebner Patricia, Wally Verena, Zauner Roland, Guttmann-Gruber Christina, Gratz Iris K, Hofbauer Josefina Piñón, Cathomen Toni, Strunk Dirk, Bauer Johann W, Koller Ulrich

Functional correction and genome integrity with duplex base editing of β-thalassemic hematopoietic stem cells

利用β-地中海贫血造血干细胞的双链碱基编辑实现功能矫正和基因组完整性

Papaioannou, Nikoletta Y; Patsali, Petros; Klermund, Julia; Papasavva, Panayiota L; Andrieux, Geoffroy; Koniali, Lola; Naiisseh, Basma; Christou, Soteroula; Sitarou, Maria; Kleanthous, Marina; Cathomen, Toni; Lederer, Carsten W

From CRISPR screens to circuits: identifying key regulators in T cell activation and state transitions

从 CRISPR 筛选到回路:识别 T 细胞活化和状态转变中的关键调控因子

Roman Azcona, Maria Silvia; Cathomen, Toni; Mussolino, Claudio

Targeted gene editing and near-universal cDNA insertion of CYBA and CYBB as a treatment for chronic granulomatous disease

靶向基因编辑和近乎普遍的 CYBA 和 CYBB cDNA 插入作为慢性肉芽肿病的治疗方法

Wolff, Jonas Holst; Skov, Thomas Wisbech; Haslund, Didde; Dorset, Sofie Rahbek; Revenfeld, Anne Louise S; Aussel, Clotilde; Jørgensen, Sofie E; Holm, Mette; Thomsen, Martin K; Ammann, Sandra; Cathomen, Toni; Mogensen, Trine H; Møller, Bjarne Kuno; Bak, Rasmus O; Mikkelsen, Jacob Giehm

The hidden risks of CRISPR/Cas: structural variations and genome integrity

CRISPR/Cas技术的潜在风险:结构变异和基因组完整性

Aussel, Clotilde; Cathomen, Toni; Fuster-García, Carla

Gene editing of CD3 epsilon to redirect regulatory T cells for adoptive T cell transfer

通过基因编辑CD3ε来重定向调节性T细胞,用于过继性T细胞转移。

Du, Weijie; Noyan, Fatih; McCallion, Oliver; Drosdek, Vanessa; Kath, Jonas; Glaser, Viktor; Fuster-Garcia, Carla; Yang, Mingxing; Stein, Maik; Franke, Clemens; Pu, Yaolin; Weber, Olaf; Polansky, Julia K; Cathomen, Toni; Jaeckel, Elmar; Hester, Joanna; Issa, Fadi; Volk, Hans-Dieter; Schmueck-Henneresse, Michael; Reinke, Petra; Wagner, Dimitrios L

Off-target effects in CRISPR-Cas genome editing for human therapeutics: Progress and challenges

CRISPR-Cas基因组编辑技术在人类治疗中的脱靶效应:进展与挑战

Kalter, Nechama; Fuster-García, Carla; Silva, Alfredo; Ronco-Díaz, Víctor; Roncelli, Stefano; Turchiano, Giandomenico; Gorodkin, Jan; Cathomen, Toni; Benabdellah, Karim; Lee, Ciaran; Hendel, Ayal

Engineering with care: safety assessment platforms for CRISPR-modified natural killer cells

谨慎的工程设计:CRISPR 修饰的自然杀伤细胞的安全评估平台

Fazeli, Alieh; Ullrich, Evelyn; Cathomen, Toni; Bexte, Tobias