Toxicology and Pharmacology of an AAV Vector Expressing Codon-Optimized RPGR in RPGR-Deficient Rd9 Mice
在RPGR缺陷型Rd9小鼠中，表达密码子优化RPGR的AAV载体的毒理学和药理学研究
期刊:Human Gene Therapy Clinical Development
影响因子:
doi:10.1089/humc.2018.168
Song, Chunjuan; Conlon, Thomas J; Deng, Wen-Tao; Coleman, Kirsten E; Zhu, Ping; Plummer, Cayrn; Mandapati, Savitri; Van Hoosear, Mailin; Green, Kari B; Sonnentag, Peter; Sharma, Alok K; Timmers, Adrian; Robinson, Paulette M; Knop, David R; Hauswirth, William W; Chulay, Jeffrey D; Shearman, Mark S; Ye, Guo-Jie
