Human iPSC-based neurodevelopmental models of globoid cell leukodystrophy uncover patient- and cell type-specific disease phenotypes
基于人类诱导多能干细胞的球状细胞脑白质营养不良神经发育模型揭示了患者和细胞类型特异性的疾病表型
期刊:Stem Cell Reports
影响因子:5.1
doi:10.1016/j.stemcr.2021.04.011
Mangiameli, Elisabeth; Cecchele, Anna; Morena, Francesco; Sanvito, Francesca; Matafora, Vittoria; Cattaneo, Angela; Della Volpe, Lucrezia; Gnani, Daniela; Paulis, Marianna; Susani, Lucia; Martino, Sabata; Di Micco, Raffaella; Bachi, Angela; Gritti, Angela