日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Long-term mitapivat treatment is safe and efficacious in patients with sickle cell disease

长期服用米塔匹伐治疗对镰状细胞病患者安全有效。

Conrey, Anna; Asomaning, Nancy; Frey, Ingrid; Charles, Ruth Pierre; Lovins, Dianna; Xu, Julia Z; Mendez-Marti, Sebastian; Le, Kang; Kruah, Britney; Li, Quan; Dunkelberger, Emily; Cellmer, Troy; Yates, Amber; Wind-Rotolo, Megan; Huston, Chris; Jeffries, Neal; Eaton, William A; Thein, Swee Lay

Functional and multi-omics signatures of mitapivat efficacy upon activation of pyruvate kinase in red blood cells from patients with sickle cell disease

米塔匹伐特激活镰状细胞病患者红细胞中丙酮酸激酶的功能和多组学特征

D'Alessandro, Angelo; Le, Kang; Lundt, Maureen; Li, Quan; Dunkelberger, Emily B; Cellmer, Troy; Worth, Andrew J; Patil, Spurthi; Huston, Chris; Grier, Abby; Dzieciatkowska, Monika; Stephenson, Daniel; Eaton, William A; Thein, Swee Lay

In vivo measurement of RBC survival in patients with sickle cell disease before or after hematopoietic stem cell transplantation

镰状细胞病患者造血干细胞移植前后红细胞存活率的体内测量

Alexis K Leonard, Dana Furstenau, Zaina Inam, Christina Luckett, Rebecca Chu, Selami Demirci, Khaled Essawi, Bjorg Gudmundsdottir, Malikiya Hinds, Julia DiNicola, Quan Li, William A Eaton, Troy Cellmer, Xunde Wang, Swee Lay Thein, Elizabeth R Macari, Sara VanNest, Matthew M Hsieh, Melissa Bonner, Fr

Therapeutic potential of the latest oxygen affinity-modifying agent, GBT021601, for treating sickle cell disease is questionable

最新氧亲和力调节剂GBT021601治疗镰状细胞病的疗效尚存疑问。

Alaimo, Braydon; Metaferia, Belhu; Cellmer, Troy; Thein, Swee Lay; Bunn, H Franklin; Eaton, William A

Phenotypic screening of the ReFRAME drug repurposing library to discover new drugs for treating sickle cell disease

利用 ReFRAME 药物再利用库进行表型筛选,以发现治疗镰状细胞病的新药

Metaferia, Belhu; Cellmer, Troy; Dunkelberger, Emily B; Li, Quan; Henry, Eric R; Hofrichter, James; Staton, Dwayne; Hsieh, Matthew M; Conrey, Anna K; Tisdale, John F; Chatterjee, Arnab K; Thein, Swee Lay; Eaton, William A

Treatment of sickle cell disease by increasing oxygen affinity of hemoglobin

通过增加血红蛋白的氧亲和力来治疗镰状细胞病

Henry, Eric R; Metaferia, Belhu; Li, Quan; Harper, Julia; Best, Robert B; Glass, Kristen E; Cellmer, Troy; Dunkelberger, Emily B; Conrey, Anna; Thein, Swee Lay; Bunn, H Franklin; Eaton, William A

Allosteric control of hemoglobin S fiber formation by oxygen and its relation to the pathophysiology of sickle cell disease

氧气对血红蛋白S纤维形成的变构调控及其与镰状细胞病病理生理学的关系

Henry, Eric R; Cellmer, Troy; Dunkelberger, Emily B; Metaferia, Belhu; Hofrichter, James; Li, Quan; Ostrowski, David; Ghirlando, Rodolfo; Louis, John M; Moutereau, Stéphane; Galactéros, Frédéric; Thein, Swee Lay; Bartolucci, Pablo; Eaton, William A

Theoretical Simulation of Red Cell Sickling Upon Deoxygenation Based on the Physical Chemistry of Sickle Hemoglobin Fiber Formation

基于镰状血红蛋白纤维形成物理化学的脱氧时红细胞镰状化的理论模拟

Dunkelberger, Emily B; Metaferia, Belhu; Cellmer, Troy; Henry, Eric R

Kinetic assay shows that increasing red cell volume could be a treatment for sickle cell disease

动力学分析表明,增加红细胞体积可能是治疗镰状细胞病的一种方法。

Li, Quan; Henry, Eric R; Hofrichter, James; Smith, Jeffrey F; Cellmer, Troy; Dunkelberger, Emily B; Metaferia, Belhu B; Jones-Straehle, Stacy; Boutom, Sarah; Christoph, Garrott W; Wakefield, Terri H; Link, Mary E; Staton, Dwayne; Vass, Erica R; Miller, Jeffery L; Hsieh, Matthew M; Tisdale, John F; Eaton, William A

Universality of supersaturation in protein-fiber formation

蛋白质纤维形成过程中过饱和现象的普遍性

Cellmer, Troy; Ferrone, Frank A; Eaton, William A