Targeted inactivation of EWSR1 :â: FLI1 gene in Ewing sarcoma via CRISPR/Cas9 driven by an Ewing-specific GGAA promoter.
利用 Ewing 特异性 GGAA 启动子驱动的 CRISPR/Cas9 技术,靶向灭活 Ewing 肉瘤中的 EWSR1 : : FLI1 基因
期刊:Cancer Gene Therapy
影响因子:5
doi:10.1038/s41417-025-00887-8
Cervera Saint T, MartÃnez Selene, Iranzo-MartÃnez MarÃa, Notario Laura, Melero-Fernández de Mera Raquel M, Alonso Javier