Safety of AADC Gene Therapy for Moderately Advanced Parkinson Disease: Three-Year Outcomes From the PD-1101 Trial
AADC基因疗法治疗中晚期帕金森病的安全性:PD-1101试验的三年结果
期刊:Neurology
影响因子:8.5
doi:10.1212/WNL.0000000000012952
Christine, Chadwick W; Richardson, R Mark; Van Laar, Amber D; Thompson, Marin E; Fine, Elisabeth M; Khwaja, Omar S; Li, Chunming; Liang, Grace S; Meier, Andreas; Roberts, Eiry W; Pfau, Madeline L; Rodman, Josh R; Bankiewicz, Krystof S; Larson, Paul S