日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

BCMA-directed mRNA CAR T cell therapy for myasthenia gravis: a randomized, double-blind, placebo-controlled phase 2b trial

BCMA靶向mRNA CAR T细胞疗法治疗重症肌无力:一项随机、双盲、安慰剂对照的2b期试验

Vu, Tuan; Durmus, Hacer; Rivner, Michael; Shroff, Sheetal; Ragole, Thomas; Myers, Bennett; Pasnoor, Mamatha; Small, George; Karam, Chafic; Vullaganti, Mithila; Peltier, Amanda; Sahagian, Gregory; Feinberg, Marc H; Slanksy, Adam; Barnett-Tapia, Carolina; Siddiqi, Zaeem; Gwathmey, Kelly; Badruddoja, Michael A; Kamboh, Hafsa; Ruggerie, Rachel N; Fedak, Renee R; Stewart, C Andrew; Kurtoglu, Metin; Kalayoglu, Murat; Singer, Michael; Jewell, Christopher M; Miljkovic, Milos D; Dimachkie, Mazen; Mozaffar, Tahseen; Howard, James F Jr

Clinical Utility of Serum Neurofilament Light Chain in Peripheral Neuropathy

血清神经丝轻链在周围神经病变中的临床应用

Karam, Chafic

Combined clinical, structural and cellular studies discriminate pathogenic and benign TRPV4 variants.

结合临床、结构和细胞研究,可以区分致病性和良性 TRPV4 变异体

Berth Sarah H, Vo Linh, Kwon Do Hoon, Grider Tiffany, Damayanti Yasmine S, Kosmanopoulos Gage, Fox Andrew, Lau Alexander R, Carr Patrice, Donohue Jack K, Hoke Maya, Thomas Simone, Karam Chafic, Fay Alex J, Meltzer Ethan, Crawford Thomas O, Gaudet Rachelle, Shy Michael E, Hellmich Ute A, Lee Seok-Yong, Sumner Charlotte J, McCray Brett A

Anti-Myelin-Associated Glycoprotein Neuropathy: Recent Developments

抗髓鞘相关糖蛋白神经病:最新进展

Morganroth, Jennifer; Karam, Chafic

Effectiveness and Utility of Genetic Testing in Establishing a Diagnosis of Hereditary Transthyretin Amyloidosis

基因检测在确诊遗传性转甲状腺素蛋白淀粉样变性中的有效性和实用性

Singh, Akash; Wyatt, John; Théaudin, Marie; Karam, Chafic; Kasper, David; Streubel, Berthold; Frascello, Karen; Bondue, Antoine

Real-world treatment utilization in adults with chronic inflammatory demyelinating polyneuropathy in the United States

美国成人慢性炎症性脱髓鞘性多发性神经病患者的真实世界治疗利用情况

Blein, Cécile; Karam, Chafic; Arvin-Berod, Clémence; Gelinas, Deborah; Barrera-Sierra, Sergio; Syed, Hashmath Ulla T A; Ward, Charlotte; Goyal, Amit; Guptill, Jeffrey

Characteristics, Treatment Patterns, Healthcare Resource Utilization, and Costs Among Patients with Multifocal Motor Neuropathy: A US Claims Database Cohort Study

多灶性运动神经病患者的特征、治疗模式、医疗资源利用和费用:一项基于美国医疗保险索赔数据库的队列研究

Khandelwal, Nikhil; Sanchirico, Marie; Ajibade, Ade; Munshi, Kiraat; Vu, Michelle; Engel-Nitz, Nicole; Steiger, Christina; Anderson, Amy J; Karam, Chafic

Hereditary Transthyretin Amyloidosis in Patients Referred to a Genetic Testing Program

接受基因检测计划的患者中的遗传性转甲状腺素蛋白淀粉样变性

Bhatt, Kunal; Delgado, Diego H; Khella, Sami; Bumma, Naresh; Karam, Chafic; Keller, Andrew; Rosen, Andrew M; Bozas, Ana; Shea, Amy; Towne, Meghan C; Polfus, Linda M; Kaeser, Gwendolyn E; Sanjurjo, Victoria; Shah, Keyur B

Effect of efgartigimod on muscle group subdomains in participants with generalized myasthenia gravis: post hoc analyses of the phase 3 pivotal ADAPT study

efgartigimod 对全身型重症肌无力患者肌肉群亚域的影响:ADAPT 3 期关键性研究的事后分析

Bril, Vera; Howard, James F Jr; Karam, Chafic; De Bleecker, Jan L; Murai, Hiroyuki; Utsugisawa, Kimiaki; Ulrichts, Peter; Brauer, Edward; Zhao, Sihui; Mantegazza, Renato; Vu, Tuan

Treatment characteristics of patients with hereditary transthyretin amyloidosis: a cohort study

遗传性转甲状腺素蛋白淀粉样变性患者的治疗特征:一项队列研究

Qarni, Taha N; Jones, Felipe J S; Drachman, Brian; Khella, Sami; Pieretti, Janice; Bustamante, Nicolas Sarmiento; Karam, Chafic