ReNeu: A Pivotal, Phase IIb Trial of Mirdametinib in Adults and Children With Symptomatic Neurofibromatosis Type 1-Associated Plexiform Neurofibroma
ReNeu:一项针对有症状的1型神经纤维瘤病相关丛状神经纤维瘤成人和儿童的米达替尼关键性IIb期试验
期刊:Journal of Clinical Oncology
影响因子:41.9
doi:10.1200/JCO.24.01034
Moertel, Christopher L; Hirbe, Angela C; Shuhaiber, Hans H; Bielamowicz, Kevin; Sidhu, Alpa; Viskochil, David; Weber, Michael D; Lokku, Armend; Smith, L Mary; Foreman, Nicholas K; Hajjar, Fouad M; McNall-Knapp, Rene Y; Weintraub, Lauren; Antony, Reuben; Franson, Andrea T; Meade, Julia; Schiff, David; Walbert, Tobias; Ambady, Prakash; Bota, Daniela A; Campen, Cynthia J; Kaur, Gurcharanjeet; Klesse, Laura J; Maraka, Stefania; Moots, Paul L; Nevel, Kathryn; Bornhorst, Miriam; Aguilar-Bonilla, Ana; Chagnon, Sarah; Dalvi, Nagma; Gupta, Punita; Khatib, Ziad; Metrock, Laura K; Nghiemphu, P Leia; Roberts, Ryan D; Robison, Nathan J; Sadighi, Zsila; Stapleton, Stacie; Babovic-Vuksanovic, Dusica; Gershon, Timothy R