Lentiviral Engineered Fibroblasts Expressing Codon-Optimized COL7A1 Restore Anchoring Fibrils in RDEB
慢病毒工程改造的成纤维细胞表达密码子优化的COL7A1,可恢复RDEB中的锚定原纤维。
期刊:Journal of Investigative Dermatology
影响因子:5.7
doi:10.1038/JID.2015.364
Georgiadis, Christos; Syed, Farhatullah; Petrova, Anastasia; Abdul-Wahab, Alya; Lwin, Su M; Farzaneh, Farzin; Chan, Lucas; Ghani, Sumera; Fleck, Roland A; Glover, Leanne; McMillan, James R; Chen, Mei; Thrasher, Adrian J; McGrath, John A; Di, Wei-Li; Qasim, Waseem