A randomized phase I/II trial of HQK-1001, an oral fetal globin gene inducer, in β-thalassaemia intermedia and HbE/β-thalassaemia
HQK-1001（一种口服胎儿珠蛋白基因诱导剂）治疗中间型 β-地中海贫血和 HbE/β-地中海贫血的随机 I/II 期试验
期刊:British Journal of Haematology
影响因子:3.8
doi:10.1111/bjh.12304
Fucharoen, Suthat; Inati, Adlette; Siritanaratku, Noppadol; Thein, Swee L; Wargin, William C; Koussa, Suzanne; Taher, Ali; Chaneim, Nattawara; Boosalis, Michael; Berenson, Ronald; Perrine, Susan P
