Base-edited cynomolgus monkeys mimic core symptoms of STXBP1 encephalopathy
碱基编辑的食蟹猴模拟了STXBP1脑病的核心症状
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2022.03.001
Lu, Zongyang; He, Siting; Jiang, Jian; Zhuang, Ling; Wang, Yan; Yang, Guang; Jiang, Xiaoyu; Nie, Yanhong; Fu, Jiqiang; Zhang, Xiaotong; Lu, Yong; Bian, Xinyan; Chang, Hung-Chun; Xiong, Zhiqi; Huang, Xingxu; Liu, Zhen; Sun, Qiang