Induction of immune tolerance to FIX following muscular AAV gene transfer is AAV-dose/FIX-level dependent
肌肉注射腺相关病毒(AAV)基因转移后诱导对凝血因子IX(FIX)的免疫耐受性取决于AAV剂量/FIX水平。
期刊:Molecular Therapy
影响因子:12
doi:10.1038/mt.2009.25
Kelly, Meagan E; Zhuo, Jiacai; Bharadwaj, Arpita S; Chao, Hengjun