Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome
基因治疗对重症Wiskott-Aldrich综合征患者的疗效
期刊:Journal of the American Medical Association
影响因子:55
doi:10.1001/jama.2015.3253
Hacein-Bey Abina, Salima; Gaspar, H Bobby; Blondeau, Johanna; Caccavelli, Laure; Charrier, Sabine; Buckland, Karen; Picard, Capucine; Six, Emmanuelle; Himoudi, Nourredine; Gilmour, Kimberly; McNicol, Anne-Marie; Hara, Havinder; Xu-Bayford, Jinhua; Rivat, Christine; Touzot, Fabien; Mavilio, Fulvio; Lim, Annick; Treluyer, Jean-Marc; Héritier, Sébastien; Lefrère, Francois; Magalon, Jeremy; Pengue-Koyi, Isabelle; Honnet, Géraldine; Blanche, Stéphane; Sherman, Eric A; Male, Frances; Berry, Charles; Malani, Nirav; Bushman, Frederic D; Fischer, Alain; Thrasher, Adrian J; Galy, Anne; Cavazzana, Marina
