Lentiviral globin gene therapy with reduced-intensity conditioning in adults with β-thalassemia: a phase 1 trial
慢病毒珠蛋白基因治疗成人 β-地中海贫血患者的减强度预处理:一项 1 期临床试验
期刊:Nature Medicine
影响因子:58.7
doi:10.1038/s41591-021-01554-9
Farid Boulad, Aurelio Maggio, Xiuyan Wang, Paolo Moi, Santina Acuto, Friederike Kogel, Chayamon Takpradit, Susan Prockop, Jorge Mansilla-Soto, Annalisa Cabriolu, Ashlesha Odak, Jinrong Qu, Keyur Thummar, Fang Du, Lingbo Shen, Simona Raso, Rita Barone, Rosario Di Maggio, Lorella Pitrolo, Antonino Gia
代谢
微生物学
贫血
FCM
IF
IHC
MICS
Human
ITGA4