A one-base therapeutic insertion in the HBG2 distal promoter reactivates γ-globin expression.
在 HBG2 远端启动子中插入一个碱基治疗性片段可重新激活 α-珠蛋白表达
期刊:Experimental Hematology & Oncology
影响因子:13.5
doi:10.1186/s40164-025-00626-7
Bao Xiuqin, Gao Yuanyi, Chen Xiaoyi, Wang Zhongju, Feng Xiaoqin, Wang Liren, Du Jing, Ye Yuhua, Chen Feijing, Du Li, Yin Aihua, Xu Xiangmin
