CRISPR/Cas9-based double-strand oligonucleotide insertion strategy corrects metabolic abnormalities in murine glycogen storage disease type-Ia
基于 CRISPR/Cas9 的双链寡核苷酸插入策略可纠正小鼠 Ia 型糖原贮积症的代谢异常
期刊:Journal of Inherited Metabolic Disease
影响因子:3.8
doi:10.1002/jimd.12660
Samanta, Ananya; George, Nelson; Arnaoutova, Irina; Chen, Hung-Dar; Mansfield, Brian C; Hart, Christopher; Carlo, Troy; Chou, Janice Y