Comparative Evaluation of AAV8 and AAV9 Gene Therapy in Fabry Knockout (Gla(-/y)) and Symptomatic (G3S(Tg/+)Gla(-/y)) Murine Models.
在法布里病敲除(Gla(-/y))和症状性(G3S(Tg/+)Gla(-/y))小鼠模型中对 AAV8 和 AAV9 基因治疗进行比较评价
期刊:Genes
影响因子:2.8
doi:10.3390/genes16070766
Chang Fu-Pang, Lee Ya-Ting, Liu Pao-Hsung, Chen Pei-Sin, Chen Yun-Ru, Niu Dau-Ming