Common AAV gene therapy vectors show nonselective transduction of ex vivo human brain tissue.
常见的AAV基因治疗载体对离体人脑组织表现出非选择性转导
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2025.101494
McGinnis J P, Ortiz-Guzman Joshua, Guevara Maria Camila, Mallannagari Sai, Belfort Benjamin D W, Bao Suyang, Srivastava Snigdha, Morkas Maria, Ji Emily, Addison Angela, Tantry Evelyne K, Chen Sarah, Wang Ying, Chen Zihong, Katlowitz Kalman A, Lange Jeffrey J, Blessing Melissa M, Mohila Carrie A, Ljungberg M Cecilia, Aldave Guillermo, Jalali Ali, Patel Akash, Sheth Sameer A, Weiner Howard L, Gopinath Shankar, Rao Ganesh, Harmanci Akdes Serin, Curry Daniel J, Arenkiel Benjamin R