Optimized in vivo base editing restores auditory function in a DFNA15 mouse model
优化的体内碱基编辑可恢复DFNA15小鼠模型的听觉功能
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-63613-w
Wang, Man; Zhang, Ziyu; Wang, Xiaohan; Zhang, Liyan; Chen, Xiangyan; Li, Nianci; Sun, Qiuhan; Lu, Yicheng; He, Zuhong; Yang, Hongbo; Tan, Fangzhi; Qi, Jieyu; Chai, Renjie