Gene Therapy Rescues Cardiac Dysfunction in Duchenne Muscular Dystrophy Mice by Elevating Cardiomyocyte Deoxy-Adenosine Triphosphate.
基因疗法通过提高心肌细胞脱氧腺苷三磷酸水平挽救杜氏肌营养不良症小鼠的心脏功能障碍
期刊:Jacc-Basic To Translational Science
影响因子:7.2
doi:10.1016/j.jacbts.2019.06.006
Kolwicz Stephen C Jr, Hall John K, Moussavi-Harami Farid, Chen Xiolan, Hauschka Stephen D, Chamberlain Jeffrey S, Regnier Michael, Odom Guy L