Small-molecule activation of TFEB alleviates Niemann-Pick disease type C via promoting lysosomal exocytosis and biogenesis.
TFEB 小分子激活可促进溶酶体胞吐和生物合成，从而缓解尼曼-匹克病 C 型
期刊:Elife
影响因子:6.4
doi:10.7554/eLife.103137
Du Kaili, Chen Hongyu, Pan Zhaonan, Zhao Mengli, Cheng Shixue, Luo Yu, Zhang Wenhe, Li Dan
