日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Modification of the VP1u region boosts transduction of adeno-associated virus vectors for ocular gene therapy.

VP1u 区域的修饰可增强腺相关病毒载体在眼部基因治疗中的转导。

Cui Mengtian, Cheng Shun-Yun, Liang Jialing, McGowan Jackson, Xu Meiyu, Xu Guangchao, Luo Li, Wu Joae, Harman Christine D, Jacobson Amanda L, Kapeller Lydia E, Mayes Melaney A, Namkung Suk, Sharma Tapan, Leland Thomas B, Zhang Fang, Yip Mitchell, Rossmiller Brian, Xue Thomas, Chen Xiupeng, Boonying Wassamon, Lotun Anoushka, Wang Dan, Su Qin, Xie Jun, Wei Yuquan, Rothstein Ann M, Gregory-Ksander Meredith S, Komaromy Andras, Tian Bo, Lin Haijiang, Punzo Claudio, Tai Phillip W L, Gao Guangping

An siRNA targeting S6k1 identifies photoreceptor phospholipid metabolism as a contributor to lipid buildup in age-related macular degeneration.

针对 S6k1 的 siRNA 发现光感受器磷脂代谢是导致年龄相关性黄斑变性中脂质积累的因素之一。

Cheng Shun-Yun, Giguere Delaney, Kim San, Seddon Johanna M, Caiazzi Jillian, Gross Katherine, McHugh Nicholas, Echeverria Dimas, Alterman Julia F, Gray-Edwards Heather, Benatti Hector Ribeiro, Renner Lauren, Woolard Hannah, Stoddard Jonathan, McGill Trevor J, Neuringer Martha, Brush Richard S, Agbaga Martin-Paul, Khvorova Anastasia, Punzo Claudio

Role of alpha-1 antitrypsin in Bruch's membrane integrity.

α1-抗胰蛋白酶在布鲁赫膜完整性中的作用

Cheng Shun-Yun, Giguere Delaney, Silverstein Ilana, Conza Adrienne, Seddon Johanna M, Kim San, Iwata Takeshi, Mueller Christian, Punzo Claudio

Update on Viral Gene Therapy Clinical Trials for Retinal Diseases

视网膜疾病病毒基因疗法临床试验最新进展

Cheng, Shun-Yun; Punzo, Claudio